Alzheimer’s disease may be inherited more often than previously known, according to a new study that paints a clearer picture of a gene long known to be linked to the common form of dementia. The ...

For the first time, gene therapy is showing promise for treating inherited deafness, researchers reported Wednesday. A study involving six children born with a genetic defect that left them profoundly ...

Researchers have used gene editing to restore hearing in adult mice with a type of inherited hearing loss. They showed that shutting down a damaged copy of a gene called a microRNA (miRNA) enabled the ...

Results from a groundbreaking clinical trial of CRISPR gene editing in 14 individuals with a form of inherited blindness show that the treatment is safe and led to measurable improvements in 11 of the ...

Results from a small clinical study suggest that EDIT-101, a CRISPR-based gene editing therapy for an inherited form of Leber’s congenital amaurosis (LCA), is safe and efficacious. The therapy did not ...

Scientists report that gene therapy restored at least some hearing and speech for five out of six children with a rare form of genetic deafness. Gene therapy shows promise for an inherited form of ...